Uncommon Cures
Uncommon Cures
For Patients & Families

A more supportive clinical trial experience

Considering a clinical trial can come with a lot of questions. Our goal is to help patients and families feel more informed, more comfortable, and better supported throughout the study, whether participation happens in person, remotely, or through a combination of both.

What To Expect | Explore the Facility | View Current Trials

What is Uncommon Cures?

A rare disease clinical trial center designed with families in mind

Uncommon Cures is a clinical trial center focused on rare disease studies.

Patients and families may work with Uncommon Cures in different ways depending on the study. Some visits may happen at our facility, some may happen remotely, and some studies may include a mix of both. No matter the format, our team is here to make the experience easier to understand, easier to navigate, and more supportive from the start.

For many families, a clinical trial can feel unfamiliar before it even begins. The process may feel unclear, the logistics may feel overwhelming, and questions often come up at every stage along the way. At Uncommon Cures, clinical trials are our focus, and support does not depend on where study activities take place. Our goal is to provide clear communication, thoughtful coordination, and real support throughout the experience.

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  • Built around clinical trials
  • Thoughtful coordination at every step
  • Support across in-person, remote, and hybrid studies
  • Clear communication for patients and families
What to expect

What to expect

Every study is different, and participation may look different from one trial to the next. Some patients may visit our facility in person. Others may participate remotely or through a hybrid model that includes both virtual and in-person touchpoints. What does not change is the support.

Before you begin

Our team helps patients and families understand the next steps, what to expect, and how the study is structured so there is more clarity from the start.

during the study

Support may include in-person visits, virtual communication, coordination with third-party clinics, or help navigating home-based services, depending on the protocol.

Along the way

No matter where study activities take place, patients and families still have access to our team for questions, guidance, and real-time support throughout the experience.
Explore the facility

For studies that include in-person visits

Some studies include visits to our facility, while others may be remote or hybrid. For families who may be coming in person, exploring the space ahead of time can help make the experience feel more familiar and more comfortable.
Explore Our Facility Page
Current Trial Opportunities

Looking for a study?

Some patients, parents, and advocacy groups come to our website specifically to learn what studies may be active and what disease areas we are currently working in. Explore current trial opportunities below to learn more about active studies and whether there may be a fit for your family.

HARMONY Study for Patients With HCU

More About This Study

Ornithine Transcarbamylase (OTC) Deficiency Research

More About This Study

Phenylketonuria PKU Study For Patients Taking Palynziq

More About This Study

Friedreich's Ataxia Research

More About This Study
Patient & Family FAQ

Common questions from patients and families

Helpful answers to common questions about participating in a study, working with our team, and knowing what to expect along the way.
Ask Us a Question
What is a clinical trial?
A clinical trial is a research study that helps doctors and researchers learn more about a potential treatment, how it works, and whether it may be safe and effective.
Every study has different requirements. The best next step is usually to learn more about the specific trial and talk with our team about whether it may be a fit.
Before a visit, we work to help families understand the next steps, what information may be needed, and how the process works so there are fewer surprises.
No. Some studies may include visits to our facility, while others may be remote or use a hybrid approach with a mix of in-person and virtual participation.
Can we see the facility before coming?
Yes. We want families to be able to explore the space ahead of time so they can feel more comfortable and better understand the environment before arriving.
Depending on the study, participation may involve local clinics, home-based services, virtual check-ins, or a combination of settings. No matter where those activities take place, our team remains available to help guide and support you.
You can reach out through our contact form or trial interest path, and our team will help point you in the right direction.
Study opportunities vary over time. The best way to see what may be available is to review current trials or contact our team directly.

Have questions? We’re here to help.

If you are exploring a clinical trial, trying to understand next steps, or simply looking for more information, we want to help you find the right starting point.
Contact Our Team