P4A Let’s Talk Rare: The Life Science Podcast
In the latest episode of Let’s Talk Rare, Owen Bryant & Georgie Rack delve into the world of drug development in rare diseases. They are joined by the brilliant Rob Freishtat, president of Uncommon Cures. Rob brings unique insights on who the key stakeholder are in developing drugs and the many ways that we can […]
Orphan Therapeutics Accelerator Announces Foundational Partnerships
Originally published on Business Wire BOSTON–(BUSINESS WIRE)–The Orphan Therapeutics Accelerator (OTXL), a non-profit biotech organization focused on completing development and commercializing therapies for ultra-rare conditions, today announced collaborative partnerships with rare disease-focused global biotech and pharmaceutical companies, a contract development and manufacturing organization (CDMO), contract research organization (CRO), and AI-based platform providers, establishing the foundation […]
Innovations in research and treatment for rare diseases
We discuss the latest efforts to advance medical research, the new possibilities spurred by artificial intelligence and the critical role of caregivers. https://www.washingtonpost.com/video/washington-post-live/rare-diseases-presented-by-harmony-biosciences/2025/02/27/fdd36eea-84a5-4166-b435-f6c7e307d8d1_video.html